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article_metadata: 10.1016/j.ymgmr.2024.101163
article_metadata: Mol Genet Metab Rep
article_metadata: 2024 Dec 27:42:101163.
article_metadata: avalglucosidase alfa case series enzyme replacement therapy infantile-onset pompe disease japanese late-onset pompe disease
article_metadata: CC BY
article_metadata: https://pubmed.ncbi.nlm.nih.gov/39835171/
article_metadata: PMC11743810
article_metadata: 39835171
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article_metadata: 2024