Published July 7, 2021 | Version v1
Journal article Open

Implementing Outcomes‑Based Managed Entry Agreements for Rare Disease Treatments: Nusinersen and Tisagenlecleucel

  • 1. University of Edinburgh, Scotland
  • 2. Andalusian School of Public Health
  • 3. National Institute for Health and Care Excellence, England
  • 4. Zorginstituut Nederland
  • 5. Bocconi University, Italy
  • 6. National Centre for Pharmacoeconomics, Ireland
  • 7. Catholic University of the Sacred Heart, Italy
  • 8. National Institute for Health and Disability Insurance, Belgium
  • 9. Agency for HTA and Tariff System, Poland
  • 10. Sofia University, Bulgaria
  • 11. Vilnius University, Lithuania

Description

Comparison of the constructs of Outcomes-Based Managed Entry Agreements (OBMEA) for nusinersen and tisagenlecleucel in countries in Europe, Canada and Australia leading to recommendations about OBMEA implementation and the need for collaboration across countries.

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Facey 2021 OBMEA case studies published.pdf

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Additional details

Funding

European Commission
IMPACT HTA - Improved Methods and Actionable Tools for Enhancing Health Technology Assessment 779312